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Abstract

Early diagnosis of dopa-responsive dystonia (DRD) and its delineation from other dystonic syndromes is of great relevance because DRD is an eminently treatable condition. The possible relevance of the phenylalanine loading test (Phe-L) in differentiating DRD from primary focal and generalized dystonia was investigated. A marked difference in the phenylalanine/tyrosine ratio between patients with DRD and patients with other types of dystonia was observed. This indicates that Phe-L may be helpful in the differential diagnosis of dystonias.

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Information & Authors

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Published In

Neurology®
Volume 60Number 4February 25, 2003
Pages: 700-702
PubMed: 12601115

Publication History

Received: November 7, 2001
Accepted: November 5, 2002
Published online: February 25, 2003
Published in print: February 25, 2003

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Authors

Affiliations & Disclosures

O. Bandmann, MD PhD
From the Department of Neurology (Drs. Bandmann and Oertel, and M. Goertz) and Hochschulrechenzentrum (Dr. Zöfel), Philipps-University Marburg; Department of Pediatrics (Drs. Zschocke and Hoffmann), University of Heidelberg; Department of Neurology (Dr. Deuschl), University of Kiel; Department of Neurology (Dr. Jost), Deutsche Klinik für Diagnostik, Wiesbaden; Department of Neurology (Dr. Hefter), Heinrich-Heine-University, Düsseldorf; and Institute of Human Genetics (Dr. Müller), Liebig-University, Giessen, Germany.
M. Goertz
From the Department of Neurology (Drs. Bandmann and Oertel, and M. Goertz) and Hochschulrechenzentrum (Dr. Zöfel), Philipps-University Marburg; Department of Pediatrics (Drs. Zschocke and Hoffmann), University of Heidelberg; Department of Neurology (Dr. Deuschl), University of Kiel; Department of Neurology (Dr. Jost), Deutsche Klinik für Diagnostik, Wiesbaden; Department of Neurology (Dr. Hefter), Heinrich-Heine-University, Düsseldorf; and Institute of Human Genetics (Dr. Müller), Liebig-University, Giessen, Germany.
J. Zschocke, MD PhD
From the Department of Neurology (Drs. Bandmann and Oertel, and M. Goertz) and Hochschulrechenzentrum (Dr. Zöfel), Philipps-University Marburg; Department of Pediatrics (Drs. Zschocke and Hoffmann), University of Heidelberg; Department of Neurology (Dr. Deuschl), University of Kiel; Department of Neurology (Dr. Jost), Deutsche Klinik für Diagnostik, Wiesbaden; Department of Neurology (Dr. Hefter), Heinrich-Heine-University, Düsseldorf; and Institute of Human Genetics (Dr. Müller), Liebig-University, Giessen, Germany.
G. Deuschl, MD
From the Department of Neurology (Drs. Bandmann and Oertel, and M. Goertz) and Hochschulrechenzentrum (Dr. Zöfel), Philipps-University Marburg; Department of Pediatrics (Drs. Zschocke and Hoffmann), University of Heidelberg; Department of Neurology (Dr. Deuschl), University of Kiel; Department of Neurology (Dr. Jost), Deutsche Klinik für Diagnostik, Wiesbaden; Department of Neurology (Dr. Hefter), Heinrich-Heine-University, Düsseldorf; and Institute of Human Genetics (Dr. Müller), Liebig-University, Giessen, Germany.
W. Jost, MD
From the Department of Neurology (Drs. Bandmann and Oertel, and M. Goertz) and Hochschulrechenzentrum (Dr. Zöfel), Philipps-University Marburg; Department of Pediatrics (Drs. Zschocke and Hoffmann), University of Heidelberg; Department of Neurology (Dr. Deuschl), University of Kiel; Department of Neurology (Dr. Jost), Deutsche Klinik für Diagnostik, Wiesbaden; Department of Neurology (Dr. Hefter), Heinrich-Heine-University, Düsseldorf; and Institute of Human Genetics (Dr. Müller), Liebig-University, Giessen, Germany.
H. Hefter, MD
From the Department of Neurology (Drs. Bandmann and Oertel, and M. Goertz) and Hochschulrechenzentrum (Dr. Zöfel), Philipps-University Marburg; Department of Pediatrics (Drs. Zschocke and Hoffmann), University of Heidelberg; Department of Neurology (Dr. Deuschl), University of Kiel; Department of Neurology (Dr. Jost), Deutsche Klinik für Diagnostik, Wiesbaden; Department of Neurology (Dr. Hefter), Heinrich-Heine-University, Düsseldorf; and Institute of Human Genetics (Dr. Müller), Liebig-University, Giessen, Germany.
U. Müller, MD
From the Department of Neurology (Drs. Bandmann and Oertel, and M. Goertz) and Hochschulrechenzentrum (Dr. Zöfel), Philipps-University Marburg; Department of Pediatrics (Drs. Zschocke and Hoffmann), University of Heidelberg; Department of Neurology (Dr. Deuschl), University of Kiel; Department of Neurology (Dr. Jost), Deutsche Klinik für Diagnostik, Wiesbaden; Department of Neurology (Dr. Hefter), Heinrich-Heine-University, Düsseldorf; and Institute of Human Genetics (Dr. Müller), Liebig-University, Giessen, Germany.
P. Zöfel
From the Department of Neurology (Drs. Bandmann and Oertel, and M. Goertz) and Hochschulrechenzentrum (Dr. Zöfel), Philipps-University Marburg; Department of Pediatrics (Drs. Zschocke and Hoffmann), University of Heidelberg; Department of Neurology (Dr. Deuschl), University of Kiel; Department of Neurology (Dr. Jost), Deutsche Klinik für Diagnostik, Wiesbaden; Department of Neurology (Dr. Hefter), Heinrich-Heine-University, Düsseldorf; and Institute of Human Genetics (Dr. Müller), Liebig-University, Giessen, Germany.
G. Hoffmann, MD
From the Department of Neurology (Drs. Bandmann and Oertel, and M. Goertz) and Hochschulrechenzentrum (Dr. Zöfel), Philipps-University Marburg; Department of Pediatrics (Drs. Zschocke and Hoffmann), University of Heidelberg; Department of Neurology (Dr. Deuschl), University of Kiel; Department of Neurology (Dr. Jost), Deutsche Klinik für Diagnostik, Wiesbaden; Department of Neurology (Dr. Hefter), Heinrich-Heine-University, Düsseldorf; and Institute of Human Genetics (Dr. Müller), Liebig-University, Giessen, Germany.
W. Oertel, MD
From the Department of Neurology (Drs. Bandmann and Oertel, and M. Goertz) and Hochschulrechenzentrum (Dr. Zöfel), Philipps-University Marburg; Department of Pediatrics (Drs. Zschocke and Hoffmann), University of Heidelberg; Department of Neurology (Dr. Deuschl), University of Kiel; Department of Neurology (Dr. Jost), Deutsche Klinik für Diagnostik, Wiesbaden; Department of Neurology (Dr. Hefter), Heinrich-Heine-University, Düsseldorf; and Institute of Human Genetics (Dr. Müller), Liebig-University, Giessen, Germany.

Notes

Address correspondence and reprint requests to Dr. O. Bandmann, Academic Neurology Unit, E Floor Medical School, University of Sheffield, Beech Hill Road, Sheffield S10 2RX, UK; e-mail: [email protected]

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Cited By
  1. Recognizing Atypical Dopa-Responsive Dystonia and Its Mimics, Neurology Clinical Practice, 11, 6, (e876-e884), (2021)./doi/10.1212/CPJ.0000000000001125
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  3. Consensus guideline for the diagnosis and treatment of tetrahydrobiopterin (BH4) deficiencies, Orphanet Journal of Rare Diseases, 15, 1, (2020).https://doi.org/10.1186/s13023-020-01379-8
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  5. Parkinson’s disease in GTP cyclohydrolase 1 mutation carriers, Brain, 137, 9, (2480-2492), (2014).https://doi.org/10.1093/brain/awu179
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  9. Dopa-Responsive Dystonia, Movement Disorder Emergencies, (319-340), (2012).https://doi.org/10.1007/978-1-60761-835-5_24
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  10. Urinary Neopterin and Phenylalanine Loading Test as Tools for the Biochemical Diagnosis of Segawa Disease, JIMD Reports - Case and Research Reports, 2012/4, (67-75), (2012).https://doi.org/10.1007/8904_2012_144
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